National Centre for Pharmacoeconomics

National Centre for

NCPE Ireland

Risdiplam (Evrysdi™). HTA ID: 21006

Risdiplam (Evrysdi™) is indicated for the treatment of 5q spinal muscular atrophy (SMA) in patients 2 months of age and older, with a clinical diagnosis of SMA Type 1, Type 2 or Type 3 or with one to four SMN2 copies.


NCPE Assessment Process Complete
Rapid review commissioned 15/03/2021
Rapid review completed 29/03/2021
Rapid Review outcome A full HTA is recommended to assess the clinical effectiveness and cost effectiveness of risdiplam compared with the current standard of care.